Unbiased Analysis of Today's Healthcare Issues
If you were a drug manufacturer, you naturally would want to focus your research on more common, highly prevalent diseases. If there are more patients with the disease, that means more drugs that can be sold. In recent years, however, the number of so-called “orphan drugs” has increased. In the 1970s, only 10 orphan drugs…
What is a rare disease? The definition varies across countries, but according to the European Medicines Agency (EMA) rare diseases are those with a prevalence of <5 cases per 10,000 people; ultra-rare diseases are those with <1 case per 50,000 people. In most cases, rare disease must not only be rare but also severe, often…
A truly amazing and uplifting story from Kind World from WBUR about a boy with Glycogen Storage Disease Type 1b, his friend and the Chocolate Bar Book. LANTZ: Dylan is 10 years old now. But this story starts when the boys were in first grade. Dylan’s mom Debra Siegel was driving her son home from…